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gene therapy

Showing 15 posts of 52 posts found.

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Scottish borders-based Ryboquinn acquires viral delivery comany Nanogenics

July 20, 2018
Medical Communications M&A, MA, Scotland, acquisitions, gene therapy, nanogenics, ryboquinn

The Scottish biotech company Ryboquinn has acquired English partner Nanogenics Solutions in a deal worth £4.45 million. The Selkirk-based firm …

News

Novartis CEO makes mark with $8.7bn AveXis acquisition

April 9, 2018
Sales and Marketing AveXis, Novartis, biotech, drugs, gene therapy, pharma, pharmaceutical

Vas Narasimhan’s first few moves as CEO of Novartis indicate that he is not afraid to take bold risks in …

News

Spark gains approval for gene therapy, paving way for first $1m treatment

December 20, 2017
Research and Development, Sales and Marketing Spark Therapeutics, biotech, drugs, gene therapy, pharma, pharmaceutical

The FDA handed approval to Spark Therapeutics’ gene therapy for an inherited eye disorder, making it the first treatment of …

News
skin-222664_960_720

Gene therapy helps child regrow 80% of skin

November 9, 2017
Medical Communications, Research and Development biotech, drugs, gene therapy, pharma, pharmaceutical, stem cell

A young child has been brought back from the verge of death after an experimental combination of stem cell and …

News
genes

Gene therapy: Advanced treatments for a new era

March 3, 2017
Medical Communications gene therapy

Aranca discusses the considerable advances that have occured in the last few years in gene therapy.Considerable research has been conducted …

News
pfizer_credit_flickr__ceiling

Pfizer expands gene therapy operations with acquisition of Bamboo Therapeutics

August 2, 2016
Manufacturing and Production, Research and Development Pfizer, acquisition, bamboo therapeutics, gene therapy

Pfizer has announced that it has acquired gene therapy biotech Bamboo Therapeutics for an initial $150 million, with potential milestone …

News
blue_jeans

Strong early data on haemophilia gene therapy boosts Biomarin

July 28, 2016
Medical Communications, Research and Development BioMarin, gene therapy, haemophilia a

Biomarin has presented interim results from a Phase I/II study that is being hailed as positive “proof-of-concept” data for their …

News
gsk_l_rgb

GSK’s gene therapy Strimvelis gets European regulatory nod

June 1, 2016
Research and Development, Sales and Marketing EU, European Commission, GlaxoSmithKline, Strimvelis, gene therapy, regulation

UK drugmaker GlaxoSmithKline (LSE: GSK) said its gene therapy Strimvelis has secured backing from the European regulators. The European Commission …

News

Pfizer and Spark Therapeutics present early data on bio-engineered haemophilia drug

May 23, 2016
Research and Development, Sales and Marketing Pfizer, Spark Therapeutics, gene therapy, haemophilia B

Pfizer (NYSE: PFE) and Spark Therapeutics (NASDAQ: ONCE) have announced that they will present data showing encouraging signs in their …

News
biogen_idec_hillerod_2008

Biogen signs $2 billion partnership deal with UPenn for gene therapies

May 17, 2016
Research and Development, Sales and Marketing Biogen, collaboration, deal, gene therapy, research

Biogen (Nasdaq: BIIB) said it has signed a deal worth up to $2 billion with the University of Pennsylvania to …

News
blue_jeans

Bluebird Bio gene therapy posts encouraging results in treatment of rare brain disease

April 21, 2016
Medical Communications, Research and Development Bluebird Bio, Phase II, gene therapy, lenti-d, paediatric, phase 2, phase 3, phase III, rare brain disease

Bluebird bio (NASDAQ: BLUE) has announced positive interim data from a Phase II/III trial evaluating their Lenti-D gene therapy in …

News

GSK’s gene therapy for rare condition in children gets EMA backing

April 4, 2016
Research and Development, Sales and Marketing ADA-SCID, European Medicines Agency, GlaxoSmithKline, Orphan Therapy, Rare Treatment, drug trial, gene therapy

UK drug major GlaxoSmithKline (LSE: GSK) has won marketing recommendation from European regulators for its first gene therapy to treat …

News
Catapult cell therapy

Construction for new £55m cell and gene manufacturing centre in Stevenage begins

November 24, 2015
Manufacturing and Production Catapult, Cell Therapy Catapult, Hertfordshire, gene therapy, manufacturing, stevenage

The Government-backed Cell Therapy Catapult has begun the construction for its cell and gene therapy manufacturing centre.   The construction …

News
Vertex logo

Vertex’s cystic fibrosis drug gets FDA approval

July 3, 2015
Research and Development, Sales and Marketing FDA, Orkambi, Vertex, cystic fibrosis, gene therapy

Vertex Pharmaceuticals cystic-fibrosis drug Orkambi, which could treat as many as 8,500 patients in the US, has been approved by …

News
Sanofi image

Sanofi makes gene therapy move

February 13, 2015
Research and Development, Sales and Marketing Genzyme, Sanofi, Voyager Therapeutics, gene therapy, merger

Sanofi has signalled its intent to develop gene therapy treatments for nerve diseases through a $745 million deal with US …

News
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