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Nemours Children’s Health selected to conduct first gene therapy for Morquio A syndrome

May 17, 2023
Research and Development Morquio A syndrome, NIH, Nemours Children's Health, Paediatrics, gene therapy

Nemours Children’s Health, based in Delaware, US, has been chosen by the Foundation for the National Institutes of Health (FNIH) …

News

AstraZeneca announces positive results from phase 3 trial for Tagrisso plus chemotherapy

May 17, 2023
Research and Development AstraZeneca, Cancer, Oncology, Tagrisso, chemotherapy

AstraZeneca has announced positive results from the FLAURA2 phase 3 trial which showed that Tagrisso (osimertinib), in combination with chemotherapy, …

News

NICE recommends nine digital treatment options for depression and anxiety

May 17, 2023
Medical Communications NICE, Neurology, anxiety, depression, digital health, mental health

The National Institute for Health and Care Excellence (NICE) has recommended six digitally enabled therapies for adult patients with anxiety …

News

FDA grants Priority Review for Takeda’s cTTP treatment

May 17, 2023
Research and Development Biologics License Application, Cardiology, FDA, Takeda, cTTP

Japanese biopharmaceutical company Takeda has announced that the US Food and Drug Administration (FDA) has accepted its Biologics License Application …

News

RadioMedix and Orano Med complete patient enrolment for neuroendocrine cancer trial

May 16, 2023
Medical Communications Oncology, Orano Med, RadioMedix, neuroendocrine cancer, oncology

US-based RadioMedix and French Orano Med, two clinical stage radiopharmaceutical companies, have announced that the last patient has been enrolled …

News

Nido Biosciences raises $109m in funding for neurological diseases treatments

May 16, 2023
Sales and Marketing Financing, Neurology, Nido Biosciences, funding, neurology

US-based clinical-stage company Nido Biosciences has announced that is has received $109m in Seed, Series A and Series B financings, …

News

Astellas and Sony enter collaborative research agreement

May 16, 2023
Research and Development ADC, Astellas Pharma, Oncology, Sony, research agreement

Sony and Astellas Pharma have announced that they have entered into a collaborative research agreement in an attempt to discover …

News

uniQure announces sale of royalty interest in Hemgenix for up to $400m

May 16, 2023
Sales and Marketing Haematology, Hemgenix, haemophilia, royalties, uniQure

uniQure has announced that it has entered a definitive agreement to sell a portion of the royalty rights due to …

News

LaNova Medicines and AstraZeneca sign global exclusive license agreement for preclinical ADC

May 15, 2023
Research and Development ADC, AstraZeneca, LaNova Medicines, License Agreement, Oncology

Chinese biotechnology company LaNova Medicines and UK-based pharma company AstraZeneca have announced that they have signed a global exclusive license …

News

Relief Therapeutics awarded approval from Swissmedic for new GMP-compliant laboratory

May 15, 2023
Research and Development GMP, Relief Therapeutics, Swissmedic, laboratory

Swiss biopharmaceutical company Relief Therapeutics has announced that its state-of-the-art R&D laboratory in Balerna, Switzerland, has been audited and approved …

News

NICE recommends Hepcludex for NHS use to treat aggressive form of viral hepatitis

May 15, 2023
Medical Communications NHS, NICE, Virology, hepatitis

The National Institute for Health and Care Excellence (NICE) has recommended Hepcludex (bulevirtide) for the treatment of chronic hepatitis delta …

News
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FDA approves new nonhormonal medication for menopause hot flashes

May 15, 2023
Medical Communications FDA, HRT, Veozah, hot flashes, menopause

The US Food and Drug Administration (FDA) has announced its approval of Veozah (fezolinetant), an oral medication to treat moderate …

News

FDA relaxes blood donation regulations for MSM

May 12, 2023
Medical Communications FDA, HIV, HIV/AIDS, blood donation

The US Food and Drug Administration (FDA) has released updated guidance for blood donation which relaxes the rules for donations …

News
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Angelini Pharma and JCR Pharmaceuticals partner to develop new epilepsy therapies

May 12, 2023
Sales and Marketing Angelini Pharma, JCR Pharmaceuticals, Neurology, epilepsy

Angelini Pharma and JCR Pharmaceuticals have announced that they have entered into an exclusive global development and commercialisation agreement for …

News

Bellerophon Therapeutics completes phase 3 study for fibrotic interstitial lung disease drug

May 12, 2023
Medical Communications Bellerophon Therapeutics, Cardiology, clinical trial, lung disease

US clinical stage biotherapeutics company Bellerophon Therapeutics has announced that the last patient has completed its phase 3 REBUILD study, …

News

FDA advisory committee votes in support of favourable benefit-risk profile for ARS Pharmaceuticals’ allergic reaction treatment

May 12, 2023
Research and Development ARS Pharmaceuticals, Allergic Disorders, FDA, allergy

US-based biopharmaceutical company ARS Pharmaceuticals has announced that the US Food and Drug Administration (FDA)’s Pulmonary-Allergy Drug Advisory Committee (PADAC) …

News

FDA advisory committee votes in favour of OTC contraceptive pill

May 11, 2023
Medical Communications Contraception, FDA, OTC, Perrigo, contraception

Perrigo Company has announced that the US Food and Drug Administration’s (FDA) Nonprescription Drugs Advisory Committee (NDAC) and the Obstetrics, …

News

Otsuka and Lundbeck gain FDA approval for supplemental New Drug Application for dementia drug

May 11, 2023
Medical Communications FDA, Lundbeck, Neurology, Otsuka Pharmaceuticals, alzheimer's disease, dementia

Japan-based healthcare company Otsuka Pharmaceutical and Danish pharma company Lundbeck have announced that the US Food and Drug Administration (FDA) …

News

AstraZeneca’s Ultomiris approved in EU for adults firm NMOSD

May 11, 2023
Medical Communications AstraZeneca, NMOSD, Neurology, Ultomiris, neurology

AstraZeneca has announced the approval of Ultomiris (ravulizumab) in the European Union (EU) for the treatment of adult patients with …

News

FDA pre-meeting report raises concerns over Sarepta’s gene therapy for Duchenne muscular dystrophy

May 11, 2023
Medical Communications Duchenne Muscular Dystrophy, FDA, Musculo-skeletal disorder, Sarepta Therapeutics, gene therapy

The US Food and Drug Administration (FDA) has released a report in preparation for its 12 May decision on Sarepta …

News
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