Pharmafile Logo
Pharmafocus logo
Advanced Search

haemophilia

Showing 15 posts of 53 posts found.

blood-1813410_960_720

Novo Nordisk presents promising findings for haemophilia treatment

June 23, 2025
Medical Communications, Research and Development Haematology, International Society on Thrombosis and Haemostasis Congres, Novo Nordisk, clinical trial data, haemophilia, market approval

Novo Nordisk has presented data indicating that a direct switch to Mim8 (denecimig) prophylaxis treatment from emicizumab without a need …

News

Qfitlia approved by FDA to treat haemophilia A or B

March 31, 2025
Research and Development FDA, Haematology, Sanofi, haemophilia, pharma

The US Food and Drug Administration (FDA) has approved Qfitlia (fitusiran) as the first therapy in the US to treat …

News

First patients treated with HEMGENIX® (etranacogene dezaparvovec) gene therapy for haemophilia B in Denmark

January 21, 2025
Sales and Marketing CSL, Denmark, genetic, haemophilia, treatment

21 January 2025 – Copenhagen, Denmark – CSL Behring Denmark today announced that the first Danish patients with haemophilia B …

News
Press release

Results from Sanofi’s ALTUVIIIO XTEND-Kids phase 3 trial published in NEJM

July 22, 2024
Research and Development Altuviiio, Haematology, Sanofi, haemophilia

Sanofi has announced that full results from the XTEND-Kids phase 3 study were published in The New England Journal of …

News
anirudh-djo3injpaoe-unsplash_3

Pfizer’s Beqvez approved by FDA for haemophilia B treatment

April 29, 2024
Medical Communications FDA, Haematology, Pfizer, haemophilia

Pfizer has announced that the US Food and Drug Administration (FDA) has approved Beqvez (fidanacogene elaparvovec-dzkt) for the treatment of …

News
blood-1813410_960_720

FDA approves BioMarin’s Roctavian for adults with severe haemophilia A

June 30, 2023
Medical Communications BioMarin, FDA, Haematology, Roctavian, haemophilia

Global biotechnology company BioMarin Pharmaceuticals has announced that the US Food and Drug Administration (FDA) has approved Roctavian (valoctocogene roxaparvocec-rvox) …

News

uniQure announces sale of royalty interest in Hemgenix for up to $400m

May 16, 2023
Sales and Marketing Haematology, Hemgenix, haemophilia, royalties, uniQure

uniQure has announced that it has entered a definitive agreement to sell a portion of the royalty rights due to …

News
blood-75301_1280

US approval for haemophilia drug derived from genetically engineered rabbit’s milk

April 2, 2020
Sales and Marketing FDA, US, haemophilia, pharma

The FDA has announced the approval of Sevenfact, a haemophilia therapy the active ingredient from which is expressed in genetically …

News
novo_nordisk_flag

Novo Nordisk halts three haemophilia studies after participants suffer thrombotic events

March 17, 2020
Manufacturing and Production, Research and Development Novo Nordisk, haemophilia, pharma

Novo Nordisk has moved to temporarily shut down two of its Phase 3 and one of its Phase 2 clinical …

News
1024px-nhs-logo

NHS Scotland gives green light to funding haemophilia A drug Hemlibra

December 18, 2019
Research and Development NHS, haemophilia, haemophilia B, haemophilia a, nhs scotland

NHS Scotland has commissioned Hemlibra (emicizumab), by Chungai Pharma UK Ltd and Roche Products Ltd, to treat people with congenital …

News
bottles_of_factor_viii_haemophilia_treatment

Irish haemophilia A patients to get continued access to Sobi’s extended half-life factor replacement therapy

December 17, 2019
Manufacturing and Production haemophilia, haemophilia B, haemophilia a

The Republic of Ireland’s Haemophilia Product Selection and Monitoring Advisory Board (HPSMAB) and Sobi United Kingdom and Republic of Ireland, …

News
blood-1813410_960_720

NHS England to fund Hemlibra for patients with severe haemophilia

August 21, 2019
Research and Development Chugai, Hemlibra, Roche, haemophilia, pharma

NHS England is to fund Roche and Chugai Pharma UK’s haemophilia drug Hemlibra, for people with sever congenital haemophilia A …

News
roche

Roche unveils wave of strong Hemlibra data in haemophilia A with or without factor VIII inhibitors

July 9, 2019
Manufacturing and Production, Research and Development Roche, haemophilia, pharma

Roche revealed a swathe of new data on Hemlibra (emicizumab) at the International Society on Thrombosis and Haemostasis (ISTH) 2019 …

News
shutterstock

Pfizer and Sangamo’s haemophilia A gene therapy shows promise at Phase 1/2

July 8, 2019
Research and Development, Sales and Marketing Pfizer, Sangamo, haemophilia, pharma

Pfizer and Sangamo Therapeutics have shared new Phase 1/2 data for their investigational SB-525 gene therapy in the treatment of …

News
novo_flag

European approval for Novo’s Esperoct in haemophilia A

June 21, 2019
Medical Communications, Sales and Marketing Esperoct, Novo Nordisk, haemophilia, pharma

The European Commission has awarded approval to Novo Nordisk’s extended half-life factor VIII therapy Esperoct (turoctocog alfa pegol, N8-GP) for …

News
The Gateway to Local Adoption Series

Latest content

STADA and Bio-Thera’s Gotenfia receives positive CHMP opinion for autoimmune diseases

December 18, 2025

Norgine enters exclusive licensing agreement with Vir Biotechnology

December 18, 2025

Incyclix appoints Kimberly Blackwell to Board of Directors

December 17, 2025

Hansa Biopharma appoints Max Sakajja as Vice President, General Manager Europe and International

December 17, 2025

GSK’s Exdensur receives MHRA approval for asthma and rhinosinusitis

December 16, 2025