gene therapy

Showing 13 posts of 43 posts found.


Biogen signs $2 billion partnership deal with UPenn for gene therapies

May 17, 2016
Research and Development, Sales and Marketing Biogen, collaboration, deal, gene therapy, research

Biogen (Nasdaq: BIIB) said it has signed a deal worth up to $2 billion with the University of Pennsylvania to …


Bluebird Bio gene therapy posts encouraging results in treatment of rare brain disease

April 21, 2016
Medical Communications, Research and Development Bluebird Bio, Phase II, gene therapy, lenti-d, paediatric, phase 2, phase 3, phase III, rare brain disease

Bluebird bio (NASDAQ: BLUE) has announced positive interim data from a Phase II/III trial evaluating their Lenti-D gene therapy in …

GSK’s gene therapy for rare condition in children gets EMA backing

April 4, 2016
Research and Development, Sales and Marketing ADA-SCID, European Medicines Agency, GlaxoSmithKline, Orphan Therapy, Rare Treatment, drug trial, gene therapy

UK drug major GlaxoSmithKline (LSE: GSK) has won marketing recommendation from European regulators for its first gene therapy to treat …

Catapult cell therapy

Construction for new £55m cell and gene manufacturing centre in Stevenage begins

November 24, 2015
Manufacturing and Production Catapult, Cell Therapy Catapult, Hertfordshire, gene therapy, manufacturing, stevenage

The Government-backed Cell Therapy Catapult has begun the construction for its cell and gene therapy manufacturing centre.   The construction …

Vertex logo

Vertex’s cystic fibrosis drug gets FDA approval

July 3, 2015
Research and Development, Sales and Marketing FDA, Orkambi, Vertex, cystic fibrosis, gene therapy

Vertex Pharmaceuticals cystic-fibrosis drug Orkambi, which could treat as many as 8,500 patients in the US, has been approved by …

Sanofi image

Sanofi makes gene therapy move

February 13, 2015
Research and Development, Sales and Marketing Genzyme, Sanofi, Voyager Therapeutics, gene therapy, merger

Sanofi has signalled its intent to develop gene therapy treatments for nerve diseases through a $745 million deal with US …

Pfizer buys into gene therapy

December 9, 2014
Research and Development, Sales and Marketing London, Pfizer, gene therapy, haemophilia, spark, therapeutics

Pfizer has announced that it is establishing a gene therapy platform as it looks to expand its rare diseases operations. …

Orphan status for haemophilia gene therapy

January 4, 2012
Research and Development AMT, gene therapy, haemophilia

Amsterdam Molecular Therapeutics has been granted an orphan drug designation for its gene therapy for haemophilia B.The FDA’s orphan designation …

Verdict on AMT’s gene therapy expected soon

May 11, 2011
Research and Development, Sales and Marketing AMT, Amsterdam Molecular Therapeutics, gene therapy, genes

Amsterdam Molecular Therapeutics says it will shortly receive the regulatory verdict on its gene therapy Glybera. Glybera (alipogene tiparvovec) is …

Pharma manufacturing news in brief

December 7, 2010
Manufacturing and Production A5 Laboratories, Adamis Pharmaceuticals, Beximco Pharmaceuticals, Caraco Pharmaceutical, Genethon BioProd, Jiangsu Yanshen Biological Technology, Viva Pharmaceuticals, contract manufacturing, gene therapy

Our round-up of manufacturing updates includes the world’s first dedicated gene therapy facility, hefty fines for a Chinese drugmaker plus …

GSK collaborates on rare genetic diseases

October 19, 2010
Research and Development Fondazione San Raffaele, Fondazione Telethon, GlaxoSmithKline, Stem cells, gene therapy

GlaxoSmithKline has partnered with one of the biggest biomedical charities in Italy and the country’s largest private research institute to …

Gene therapy advance hailed for thalassemia

September 16, 2010
Research and Development Bluebird Bio, gene therapy, thalassemia

A new gene therapy for one of the most frequently inherited genetic disorders has produced promising results. The trial by …

Gene therapy: the tailor-made treatment

June 28, 2006
Research and Development drug development, gene therapy

 At the risk of boring my audience, I really can't help beginning with yet another attack of nostalgia ,or rather …

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